Myofibers in DMD patients undergo continuous cycles of degeneration and regeneration leading to necrosis, fibrosis and inflammation. Although loss of dystrophin protein is clearly the initiating ...
The open-label FORWARD-53 study enrolled 11 boys with DMD aged 5 to 11 years to receive infusions of WVE-N531 every 2 weeks at a dose of 10 mg/kg, with muscle biopsies taken after 24 and 48 weeks.
Medical science has long been on the hunt for a deeper understanding of the devastating scarring of the body's organs known as fibrosis, which leads to irrevocable loss of function. Fibrosis ...
The UAB Gregory Fleming James Cystic Fibrosis Research Center is a university-wide interdisciplinary research center funded by the National Institutes of Health, the Cystic Fibrosis Foundation, and ...
An international study has identified two types of these so-called dysbioses in cystic fibrosis. They display ... Landmark Study Involving Babies in Ireland Supports Use of Cystic Fibrosis Drug in ...
(NASDAQ:CAPR) announced today that it intends to file a Biologics License Application [BLA] for deramiocel for the treatment of patients with Duchenne Muscular Dystrophy [DMD] cardiomyopathy.
Inspired by the idea of creating a maskless lithography system using a digital micromirror device (DMD), [Nemo Andrea] tore into an Anycubic Photon Ultra, DLP & resin-based 3D printer to take a ...
The importance of family and community support took on a new meaning when our son Michael was diagnosed with Duchenne muscular dystrophy (DMD), a rare and severe neuromuscular disease. We started ...