Larimar Therapeutics, Inc. (NASDAQ:LRMR) released initial data from the ongoing long-term OLE study evaluating daily ...

The disorder is caused by an erroneous long chain of repeating DNA bases in the FXN gene, which prevents the cell’s transcriptional machinery from reading the entire gene and producing the ...

Early attempts to treat FRDA with antioxidants, before the FXN gene was discovered, were prompted by a generic assumption that oxidative stress contributes to neurodegeneration, as well as by the ...

In the assessment of 12-month price targets, analysts unveil insights for Voyager Therapeutics, presenting an average target ...

inherited neuromuscular disease caused by mutations in a gene called FXN that leads to impaired muscle coordination, as well as problems with the heart and central nervous system. Earlier this ...

inherited neuromuscular disease caused by mutations in a gene called FXN that leads to impaired muscle coordination, as well as problems with the heart and central nervous system. Earlier this ...

Treatment with nomlabofusp modified gene expression and lipid profiles in addition to increasing frataxin – FXN – levels in study participants with Friedreich’s ataxia. Modeling and ...