An experimental gene therapy might one day give people with heart failure a new lease on life. The therapy prompted the pigs’ ...

Researchers found a genetic therapy that could be used to reverse heart failure. A recent study found that it worked on large ...

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model.

Researchers suggest an application to FDA may be made within the next 12 months, requesting approval to carry out a human clinical trial with the gene therapy.

Ultragenyx Pharmaceutical RARE announced that it has submitted a biologics license application (BLA) to the FDA for its UX111 ...

The new gene therapy, reported in a npj Regenerative Medicine paper, prevented heart failure from worsening and even improved some key measures of heart function in pig models.

They are both members of the Pediatric Gene Therapy & Medical Ethics Working Group in the department of medical ethics at the NYU Grossman School of Medicine. On Nov. 18, a female pediatric ...

In her years-long effort to develop a gene therapy for her 7-year-old son Maxwell, Amber Freed has tried most of the usual fundraising tricks: A foundation, GoFundMe campaigns, lemonade stands ...