Recognizing that Duchenne muscular dystrophy is one of the most common pediatric genetic rare diseases, the General Assembly decided to designate 7 September, the current World Duchenne Awareness ...

Duchenne's Muscular Dystrophy is an aggressive form of genetic muscular dystrophy that 8-year-old Ryan was diagnosed with in February. The Fundraiser called 'Rally for Ryan' at the Eagle Hose ...

Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following ... could become the second genetic medicine for Duchenne ...

Duchenne, one of the most severe forms of muscular dystrophy, affects about one out of every 3,600 boys. The inherited rare disease on the X chromosome is caused by a genetic defect and it ...

Duchenne muscular dystrophy is the most common early onset form of muscular dystrophy; many boys become wheelchair bound in their teens and die ... patient's cells to correct genetic diseases ...

A new technology that delivers two halves of a gene separately could enable gene therapy treatments of muscular dystrophies.