Since the isolation of the gene that causes Duchenne muscular dystrophy (DMD), scientists have progressed in understanding ...
Duchenne muscular dystrophy is the most common early onset form of muscular dystrophy; many boys become wheelchair bound in their teens and die ... patient's cells to correct genetic diseases ...
A new technology that delivers two halves of a gene separately could enable gene therapy treatments of muscular dystrophies.
Recognizing that Duchenne muscular dystrophy is one of the most common pediatric genetic rare diseases, the General Assembly decided to designate 7 September, the current World Duchenne Awareness ...
In recent years, a growing understanding of myotonic dystrophy type 1 (DM1 ... Like many other muscular dystrophies, the cause of DM1 is genetic. An alteration in the causative gene, dystrophia ...
Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following ... could become the second genetic medicine for Duchenne ...
Duchenne's Muscular Dystrophy is an aggressive form of genetic muscular dystrophy that 8-year-old Ryan was diagnosed with in February. The Fundraiser called 'Rally for Ryan' at the Eagle Hose ...