Muscular Dystrophy News8d
Taking control when living with limb-girdle muscular dystrophy
Columnist Patrick Moeschen, who lives with limb-girdle muscular dystrophy, explains why controlling what he can is so ...
Business Insider26d
AskBio Receives FDA Rare Pediatric Disease and Orphan-Drug Designations for AB-1003 for the Treatment of Limb-Girdle Muscular Dystrophy Type 2I/R9
for the treatment of limb-girdle muscular dystrophy type 2I/R9 (LGMD2I/R9). FDA grants rare pediatric disease designation to incentivize the development of new treatments for serious and life ...
Eagle-Tribune22d
IND for ATA-200, a Gene Therapy for the Treatment of Limb-Girdle Muscular Dystrophy Type 2C/R5 (LGMD2C/R5), cleared to proceed by FDA
ATA-200 is a one-time gene therapy for the treatment of γ-sarcoglycan related limb-girdle muscular dystrophy Type 2C/R5 (LGMD2C/R5), a serious and debilitating condition that affects children and ...
Yahoo Finance4d
Limb-Girdle Muscular Dystrophy (LGMD) Competitive Landscape Report 2024
No disease-modifying treatment has proven to alter LGMD ... contributed to an equal number of deals. The Limb-Girdle Muscular Dystrophy: Competitive Landscape combines data from the Pharma ...
Financial Post27d
AskBio Receives FDA Rare Pediatric Disease and Orphan-Drug Designations for AB-1003 for the Treatment of Limb-Girdle Muscular Dystrophy Type 2I/R9
Asklepios BioPharmaceutical, Inc. (AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, today announced that AB-1003 (also known as LION-101) has ...
Mena FN26d
Askbio Receives FDA Rare Pediatric Disease And Orphan-Drug Designations For AB-1003 For The Treatment Of Limb-Girdle Muscular Dystrophy Type 2I/R9
Limb-Girdle Muscular Dystrophy Type 2I – Summary. Available at: Last accessed: November 2024. [4] Chu ML, Moran E. The Limb-Girdle Muscular Dystrophies: Is Treatment on the Horizon ...