Despite disappointing results in the genetic neurodegenerative disorder, the drug shows potential for treating obesity.

Genetic disorders are diseases caused by an abnormal gene, often described as a mutation. When such diseases are inherited (rather than the result of a random mutation), it means they are passed along ...

Bio­haven’s stock fell in pre­mar­ket trad­ing on Mon­day af­ter it an­nounced a Phase 3 tri­al fail­ure of its myo­statin in­hibitor in spinal mus­cu­lar at­ro­phy and … ...

The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...

35% of subjects had no measurable levels of myostatin at baseline and had imbalances in some genetic factors. In the RESILIENT SMA study, taldefgrobep showed clinically meaningful improvements in ...

Nov. 19, 2024 — Researchers have found that coronaviruses like SARS-CoV-2 contain genes that appear important for viral survival even though they don't produce a ... Innovative Approach Maps ...