Pompe disease will always be a form of muscular dystrophy that deteriorates the muscles throughout the body causing muscle weakness. The science of it will never change, but the treatment is something ...

Koeberl’s research focuses on using adeno-associated virus (AAV) vectors to insert DNA or RNA into targeted cells where it can repair faulty genes that cause disease. Pompe disease is triggered by ...

Treating chronic disease has proven difficult because there is not one simple cause, like a single gene mutation, that a treatment could target. At least, that's how it has appeared to scientists ...

Nov. 27, 2024 — The food additive carrageenan (E 407) can be responsible for the development of chronic inflammatory bowel disease, ulcers, and increased blood sugar levels in animals.

Fintel reports that on November 26, 2024, RBC Capital initiated coverage of Avidity Biosciences (NasdaqGM:RNA) with a ...

Chronic diseases like type 2 diabetes and inflammatory disorders have a huge impact on humanity. They are a leading cause of disease burden and deaths around the globe, are physically and ...

A precancerous cell is a cell with certain abnormalities that makes it more likely to become ... Chronic (persistent) inflammation can lead to precancerous changes in tissues. An example is ...

Eculizumab treatment may reduce the symptoms of neuromyelitis optica spectrum disorder (NMOSD) in the acute phase of the disease, a study found. Seladelpar treatment leads to sustained efficacy and ...

Moreno concurs: "In school, we're taught to consider changes in protein structure or DNA sequences when looking for causes of disease, but we've demonstrated that those are not the only ...

enabling their isolation from stem cell differentiation cultures, advancing future disease modeling, drug discovery, and biological pacemaker applications. Intrinsic regulators of stem cell-based ...

Cell adhesion is the process by which cells form contacts with each other or with their substratum through specialized protein complexes. Intercellular adhesion can be mediated by adherens ...