The result of the NEXUS trial means that the two companies can now press on with their plan to refile for EU approval of the ...

Minoryx Therapeutics, a late-stage biotech company focused on the development of therapies for orphan central nervous system (CNS) disorders and Neuraxpharm Group (Neuraxpharm), a leading European ...

Myriad Genetics, Inc. (NASDAQ: MYGN), a leader in genetic testing and precision medicine, announced the election of Mark S.

Sickle cell disease is an inherited genetic condition, explained Dr. Férol Gbénou. It is characterized by abnormal hemoglobin, which can block blood flow and cause pain and organ damage.

Two of Ruth McDonnell's sons suffered from the same rare neurological condition and Make-A-Wish provided both boys with gifts ...

The FDA last week announced that it is looking into the safety of bluebird bio ’s gene therapy Skysona (elivaldogene ...

Aedrik Quinn, 8, has the rare life-threatening disease cerebral adrenoleukodystrophy (ALD). This is the first of a series of ...

4) FASTK inhibits SIRT1 expression to aggravate ALD, while Dnajc10 promotes Nrf2 to alleviate ALD. 5) ALDH2 can effectively metabolize toxic aldehydes and slow down the progression of liver disease.

Tardive dyskinesia shares features with other movement disorders, such as Tourette syndrome ... Its exact causes are unknown, but genetics, changes in brain function and structure, and ...

Rachel Maddow sums up the story of how RFK Jr. is seen as largely responsible for an explosion of measles cases on the island ...

Genetics of Ald and Nafld: Why Bother? Chronic liver disease related to ALD and NAFLD weighs heavily on the health care systems of the developed world. They already account for the majority of ...

Genetic disorders are diseases caused by an abnormal gene, often described as a mutation. When such diseases are inherited (rather than the result of a random mutation), it means they are passed along ...