Bhopal, Bhopal resident Sharda Yadav's life is confined to one room where she looks after her two sons, in their mid and late 20s, who are congenitally disabled, a disorder linked to exposure of their ...
At the Breakthroughs in Muscular Dystrophy special meeting held in Chicago Nov. 19-20, 2024, and organized by the American Society of Gene & Cell Therapy (ASGCT), multiple interventions at the RNA ...
As a child, Michael Rudnicki liked to dismantle clocks. He would take them apart, piece by piece, to see what made them tick. That curiosity has been a driving force throughout the celebrated ...
Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following treatment with its experimental gene therapy. The positive ...
What is FSHD in children? Facioscapulohumeral muscular dystrophy (FSHD) is a rare genetic muscle disease that affects the muscles of your child’s face, shoulders, upper arms, and lower legs. These ...