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What is FSHD in children? Facioscapulohumeral muscular dystrophy (FSHD) is a rare genetic muscle disease that affects the muscles of your child’s face, shoulders, upper arms, and lower legs. These ...

Regenxbio reported Monday the first clinical evidence showing improved muscle function in boys with Duchenne muscular dystrophy following treatment with its experimental gene therapy. The positive ...

It is the third most common muscular dystrophy and affects the muscles in the face, clavicle, shoulder, and legs. Limb-Girdle Muscular Dystrophy Life Expectancy Limb-girdle muscular dystrophy does not ...

PROGRESSIVE muscular dystrophy was recognized over a century ago, and Gowers noted its familial occurrence soon afterward. The disease, which is similar in affected members of a family ...

Tina Fegley, who has a form of Limb-girdle muscular dystrophy and uses a wheelchair, admits to PEOPLE that navigating the dating world hasn’t been easy. “I feel like most guys would see the ...

The most common type of muscular dystrophy is called 'Duchenne' type. Here are its signs and symptoms: Myotonic, congenital, limb-girdle, facioscapulohumeral aka FSHD are a few other types of the ...

(AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, announced that AB-1003 (also known as LION-101) has received rare paediatric disease designation ...

This would be regarding the development of gene therapy SRP-9003 [bidridistrogene xeboparvovec] for the treatment of patients with limb-girdle muscular dystrophy [LGMD]. As I will explain below ...

But clearly Trump and his surrogates saw incredible value in tapping into a podcast ecosystem that has large numbers of young male listeners who otherwise might have skipped casting ballots.

Sarepta has a focus on RNA-based therapies such as exon skipping antisense oligonucleotide (ASO) therapies, gene therapies and gene editing, primarily for Duchenne muscular dystrophy, but also other ...