First-ever FDA approval for gene therapy directly administered to the brain - - Priority review voucher granted - - Broad label including children and adults - - ...
MeiraGTx Holdings plc (Nasdaq: MGTX), a vertically integrated, clinical stage genetic medicines company, today announced financial and operational results for the third quarter ended September 30, ...
The company plans to monetize the voucher. About aromatic L-amino acid decarboxylase (AADC ... the outcome of pricing, coverage and reimbursement negotiations with third party payors for PTC's ...